Category: Gene therapy

Gene therapy, stem cell therapy, CAR T, cell therapy, and gene editing are all forms of genomic medicine1 – an approach to cure and treat human diseases that uses human biology rather than chemical compounds made in the lab.

The ability to consistently bring treatments and cures to market depends upon a company’s capacity to create and sustain a successful product development pipeline.

Written for and originally published on AGT Big Picture  Gene therapy, stem cell therapy, CAR-T, cell therapy and gene editing […]

Historically, developing rare disease cures and treatments has been challenging. The small, globally dispersed patient population made it difficult and […]